Globin gene transfer as a potential treatment for the beta-thalassaemias and sickle cell disease.
Sadelain
M
M
Laboratory of Gene Transfer and Gene Expression, Memorial Sloan-Kettering Cancer Center, New York, NY 10021, USA. m-sadelain@ski.mskcc.org
D000755:Anemia, Sickle Cell / Q000628:therapy*; D000818:Animals; D004195:Disease Models, Animal; D018014:Gene Transfer Techniques; D015316:Genetic Therapy / Q000379:methods*; D005914:Globins / Q000235:genetics*; D006801:Humans; D016086:Lentivirus / Q000378:metabolism; D051379:Mice; D008957:Models, Genetic; D019076:Transgenes; D017086:beta-Thalassemia / Q000628:therapy*
D005914:Globins