Gene therapy for hemophilia? Yes.
Negrier
C
C
Haemophilia Center, Edouard Herriot University Hospital, University of Lyon, 69003 Lyon, France. claude.negrier@chu-lyon.fr
D005164:Factor IX / Q000235:genetics; D005169:Factor VIII / Q000235:genetics; D018014:Gene Transfer Techniques; D015316:Genetic Therapy / Q000379:methods*; D006467:Hemophilia A / Q000628:therapy*; D006801:Humans; D019076:Transgenes
C078147:F8 protein, human; D005169:Factor VIII; D005164:Factor IX