Duchenne muscular dystrophy and dystrophin: pathogenesis and opportunities for treatment.
MRC Functional Genetics Unit, University of Oxford, South Parks Road, Oxford OX1 3QX, UK.
Kristen J
KJ
Nowak
Kay E
KE
Davies
D016189:Dystrophin / Q000502:physiology*; D015316:Genetic Therapy; D006801:Humans; D020388:Muscular Dystrophy, Duchenne / Q000503:physiopathology* / Q000628:therapy*; D032446:Myoblasts / Q000637:transplantation; D016376:Oligonucleotides, Antisense / Q000627:therapeutic use; D061988:Proteasome Inhibitors; D033581:Stem Cell Transplantation; D015854:Up-Regulation / Q000502:physiology
D016189:Dystrophin; D016376:Oligonucleotides, Antisense; D061988:Proteasome Inhibitors