Introduction. Advances in Gaucher Disease: therapeutic goals and evaluation and monitoring guidelines.
Weinreb
Neal J
NJ
International Collaborative Gaucher Group, University Research Foundation for Lysosomal Storage Diseases, Inc., Coral Springs, FL, USA.
D005776:Gaucher Disease / Q000175:diagnosis / Q000266:history / Q000628:therapy*; D049672:History, 19th Century; D049673:History, 20th Century; D049674:History, 21st Century; D006801:Humans; D007391:International Cooperation; D017410:Practice Guidelines as Topic; D012042:Registries