[An opening in Duchenne muscular dystrophy: persistent therapeutic rescue of dystrophin by vectorized antisense mediated exon skipping in mdx mice].
Goyenvalle
Aurélie
A
Vulin
Adeline
A
Fougerousse
Françoise
F
Leturcq
France
F
Kaplan
Jean-Claude
JC
Garcia
Luis
L
Danos
Olivier
O
D000818:Animals; D016189:Dystrophin / Q000235:genetics; D005091:Exons / Q000235:genetics; D015316:Genetic Therapy / Q000379:methods; D051379:Mice; D018101:Mice, Inbred mdx; D020388:Muscular Dystrophy, Duchenne / Q000628:therapy*
D016189:Dystrophin