Efficacy of gene therapy for SCID is being confirmed.
Cavazzana-Calvo
Marina
M
Département de Biothérapie, Hôpital Necker-Enfants Malades, 75015 Paris, France. m.cavazzana@nck.ap-hop-paris.fr
Fischer
Alain
A
D000243:Adenosine Deaminase / Q000172:deficiency; D018952:Antigens, CD34 / Q000032:analysis; D001854:Bone Marrow Cells / Q000276:immunology; D016026:Bone Marrow Transplantation; D017988:Gammaretrovirus; D018014:Gene Transfer Techniques; D040181:Genetic Diseases, X-Linked / Q000628:therapy*; D015316:Genetic Therapy / Q000009:adverse effects / Q000379:methods; D005822:Genetic Vectors; D006801:Humans; D007111:Immunity, Cellular; D053631:Interleukin Receptor Common gamma Subunit; D020395:Receptors, Interleukin-7 / Q000235:genetics; D016511:Severe Combined Immunodeficiency / Q000235:genetics / Q000276:immunology / Q000628:therapy*; D014161:Transduction, Genetic
D018952:Antigens, CD34; C507941:IL2RG protein, human; D053631:Interleukin Receptor Common gamma Subunit; D020395:Receptors, Interleukin-7; D000243:Adenosine Deaminase