Report on a Round Table Conference in Monaco on 17th and 18th January, 2004.
Duchenne Parent Project France and the Association Monegasque Contre les Myopathies invited 35 scientists and representatives of Duchenne parent groups for this Round-Table Conference in Monaco. Two scientific approaches towards the treatment of Duchenne muscular dystrophy were discussed. The following text is not a scientific report for experts but was written for the families with Duchenne boys in January and February 2004. Some of the experiments are described in greater detail, because this report should make it clear that in spite of the incredible complexity of the human genetic structure, new experimental techniques and the skill of the scientists make it possible to manipulate the information of the very large dystrophin gene without interfering with the other about 25,000 to 30,000 genes in every cell of a Duchenne boy.
Scheuerbrandt
Günter
G
gscheuerbrandt@t-online.de
D000818:Animals; D003062:Codon; D006801:Humans; D008297:Male; D051379:Mice; D018101:Mice, Inbred mdx; D008984:Monaco; D020388:Muscular Dystrophy, Duchenne / Q000235:genetics* / Q000628:therapy*; D009154:Mutation
D003062:Codon