title: Orphan drugs and orphan tests in the USA.
authors.affiliation: Hayward Genetics Center, Tulane University School of Medicine, New Orleans, LA 70112, USA. jthoene@tulane.edu
authors.forename: Jess G
authors.initials: JG
authors.lastname: Thoene
mesh_terms: D004345:Drug Industry / Q000331:legislation & jurisprudence*; D006801:Humans; D007880:Legislation, Drug; D009965:Orphan Drug Production / Q000331:legislation & jurisprudence*; D035583:Rare Diseases / Q000188:drug therapy*; D014481:United States; D014486:United States Food and Drug Administration