Gene therapy: the 'pro-sense' approach to Duchenne muscular dystrophy.
van Deutekom
Judith C T
JC
Center for Human and Clinical Genetics, Leiden University Medical Center, Wassenaarseweg 72, 2333 AL Leiden, The Netherlands. deutekom@lumc.nl
D000818:Animals; D016189:Dystrophin / Q000096:biosynthesis / Q000235:genetics; D005091:Exons; D015316:Genetic Therapy; D006801:Humans; D051379:Mice; D020388:Muscular Dystrophy, Duchenne / Q000235:genetics* / Q000628:therapy*; D020320:Oligoribonucleotides, Antisense / Q000627:therapeutic use*; D012342:RNA, Small Nuclear / Q000627:therapeutic use; D013489:Suppression, Genetic
D016189:Dystrophin; D020320:Oligoribonucleotides, Antisense; D012342:RNA, Small Nuclear