title: Orphan drugs provide needed treatment options.
authors.affiliation: airPharma, USA. Sraskin@mcmedsoc.org
authors.forename: Robert J
authors.initials: RJ
authors.lastname: Dockhorn
mesh_terms: D000163:Acquired Immunodeficiency Syndrome / Q000188:drug therapy; D000328:Adult; D002648:Child; D003550:Cystic Fibrosis / Q000188:drug therapy; D016527:Drug Costs; D005260:Female; D006801:Humans; D007223:Infant; D007231:Infant, Newborn; D008297:Male; D009103:Multiple Sclerosis / Q000188:drug therapy; D009965:Orphan Drug Production / Q000191:economics / Q000331:legislation & jurisprudence; D010344:Patient Advocacy; D012109:Research Support as Topic; D005879:Tourette Syndrome / Q000188:drug therapy; D014481:United States; D014486:United States Food and Drug Administration