title: Gene therapy of storage disorders by retroviral and lentiviral vectors.
authors.affiliation: San Raffaele Telethon Institute for Gene Therapy and Vita Salute University, H. San Raffaele Scientific Institute, Milan 20132, Italy.
authors.forename: Alessandra
authors.initials: A
authors.lastname: Biffi
authors.forename: Luigi
authors.initials: L
authors.lastname: Naldini
mesh_terms: D000818:Animals; D015316:Genetic Therapy / Q000379:methods; D005822:Genetic Vectors / Q000235:genetics / Q000627:therapeutic use*; D018380:Hematopoietic Stem Cell Transplantation; D006801:Humans; D016086:Lentivirus / Q000235:genetics; D016464:Lysosomal Storage Diseases / Q000235:genetics / Q000628:therapy*; D009474:Neurons / Q000637:transplantation; D014161:Transduction, Genetic