Neuromuscular disorders: orphan diseases deserve attention.
de Visser
Marianne
M
Department of Neurology, Academic Medical Centre, University of Amsterdam, Meibergdreef 9, 1105 AZ, Amsterdam, Netherlands. m.devisser@amc.uva.nl
D006801:Humans; D009468:Neuromuscular Diseases / Q000188:drug therapy*; D009965:Orphan Drug Production / Q000379:methods*; D035583:Rare Diseases / Q000188:drug therapy*