Design of phase III clinical trials for treatments of orphan retinal diseases: an overview of considerations.
Hyman
Leslie
L
Preventive Medicine and Ophthalmology in the Department of Preventive Medicine, Division of Epidemiology, Stony Brook University, Stony Brook, New York, NY, USA.
D017326:Clinical Trials, Phase III as Topic / Q000379:methods*; D015785:Eye Diseases, Hereditary / Q000235:genetics / Q000628:therapy*; D006801:Humans; D035583:Rare Diseases / Q000235:genetics / Q000628:therapy*; D012107:Research Design; D012164:Retinal Diseases / Q000235:genetics / Q000628:therapy*