title: Design of phase III clinical trials for treatments of orphan retinal diseases: an overview of considerations.
authors.affiliation: Preventive Medicine and Ophthalmology in the Department of Preventive Medicine, Division of Epidemiology, Stony Brook University, Stony Brook, New York, NY, USA.
authors.forename: Leslie
authors.initials: L
authors.lastname: Hyman
mesh_terms: D017326:Clinical Trials, Phase III as Topic / Q000379:methods*; D015785:Eye Diseases, Hereditary / Q000235:genetics / Q000628:therapy*; D006801:Humans; D035583:Rare Diseases / Q000235:genetics / Q000628:therapy*; D012107:Research Design; D012164:Retinal Diseases / Q000235:genetics / Q000628:therapy*