title: Challenges associated with clinical trials for inherited and orphan retinal diseases.
authors.affiliation: Department of Ophthalmology and Electrophysiology at the University of Illinois, Chicago Eye Center, Chicago, IL, USA.
authors.forename: Gerald A
authors.initials: GA
authors.lastname: Fishman
mesh_terms: D002986:Clinical Trials as Topic; D015785:Eye Diseases, Hereditary / Q000235:genetics / Q000628:therapy*; D006801:Humans; D018579:Patient Selection; D035583:Rare Diseases / Q000235:genetics / Q000628:therapy*; D012164:Retinal Diseases / Q000235:genetics / Q000628:therapy*; D016896:Treatment Outcome