Increasing importance of stem cell gene therapy in adenosine deaminase deficiency?
Ozdemir
Oner
O
Niehues
D000243:Adenosine Deaminase / Q000172:deficiency* / Q000627:therapeutic use; D000818:Animals; D015316:Genetic Therapy; D006801:Humans; D051379:Mice; D033581:Stem Cell Transplantation
D000243:Adenosine Deaminase; C051409:pegademase bovine