Uncertain miracle: a biotech drug extends a life, but at what price? For Ms. Lees, treatment bill now totals $7 million; her bones keep crumbling; guilt of another $1,400 day.
D001709:Biotechnology; D017281:Cost of Illness; D005382:Financing, Personal; D005776:Gaucher Disease / Q000188:drug therapy*; D005962:Glucosylceramidase / Q000191:economics* / Q000627:therapeutic use*; D006801:Humans; D007221:Industry / Q000191:economics*; D007349:Insurance, Health, Reimbursement; D009965:Orphan Drug Production / Q000191:economics*; D011788:Quality of Life; D035583:Rare Diseases / Q000188:drug therapy*; D014481:United States
D005962:Glucosylceramidase; C090568:imiglucerase