Damage at the cellular and organ levels in LSDs: possibility for prevention/reversibility with ERT.
Cox
Timothy M
TM
Department of Medicine, University of Cambridge, Addenbrooke's Hospital, Cambridge, UK. jbg20@medschl.cam.ac.uk
Beck
Michael
M
D000818:Animals; D003928:Diabetic Nephropathies / Q000453:epidemiology; D004195:Disease Models, Animal; D006801:Humans; D016464:Lysosomal Storage Diseases / Q000188:drug therapy / Q000503:physiopathology / Q000517:prevention & control*; D012307:Risk Factors