title: Jumpstarting research into neglected diseases.
abstract: Unwilling to wait and hope for a cure, patients suffering from rare or little-studied diseases and their families are galvanizing research efforts and driving innovative approaches to develop new treatments.
authors.affiliation: Portland, Oregon.
authors.forename: Mitchell
authors.initials: M
authors.lastname: Leslie
mesh_terms: D035843:Biomedical Research / Q000191:economics / Q000639:trends*; D004345:Drug Industry / Q000191:economics; D006801:Humans; D009965:Orphan Drug Production / Q000191:economics / Q000331:legislation & jurisprudence; D010361:Patients; D004364:Pharmaceutical Preparations / Q000191:economics / Q000600:supply & distribution; D035583:Rare Diseases / Q000188:drug therapy* / Q000191:economics
chemical_list: D004364:Pharmaceutical Preparations