title: Therapeutic options for patients with severe beta-thalassemia: the need for globin gene therapy.
authors.affiliation: Gene Transfer and Gene Expression Laboratory, Department of Medicine and Immunology Program, Memorial Sloan-Kettering Cancer Center, New York, NY 10021, USA. m-sadelain@ski.mskcc.org
authors.forename: Michel
authors.initials: M
authors.lastname: Sadelain
authors.forename: Farid
authors.initials: F
authors.lastname: Boulad
authors.forename: Renzo
authors.initials: R
authors.lastname: Galanello
authors.forename: Patricia
authors.initials: P
authors.lastname: Giardina
authors.forename: Franco
authors.initials: F
authors.lastname: Locatelli
authors.forename: Aurelio
authors.initials: A
authors.lastname: Maggio
authors.forename: Stefano
authors.initials: S
authors.lastname: Rivella
authors.forename: Isabelle
authors.initials: I
authors.lastname: Riviere
authors.forename: John
authors.initials: J
authors.lastname: Tisdale
mesh_terms: D000818:Animals; D015316:Genetic Therapy / Q000379:methods; D005914:Globins / Q000235:genetics*; D006801:Humans; D051379:Mice; D017086:beta-Thalassemia / Q000235:genetics / Q000473:pathology / Q000628:therapy*
chemical_list: D005914:Globins