Low-dose versus high-dose therapy for Gaucher disease: Goals and markers.
Hollak
Carla E M
CE
de Fost
Maaike
M
Aerts
Johannes M F G
JM
vom Dahl
Stephan
S
D000273:Adipose Tissue / Q000473:pathology; D015415:Biomarkers; D001853:Bone Marrow / Q000473:pathology; D004305:Dose-Response Relationship, Drug; D004341:Drug Evaluation / Q000592:standards; D005776:Gaucher Disease / Q000188:drug therapy* / Q000201:enzymology / Q000473:pathology; D005962:Glucosylceramidase / Q000008:administration & dosage* / Q000627:therapeutic use; D006596:Hexosaminidases / Q000097:blood; D006801:Humans; D008099:Liver / Q000473:pathology; D008279:Magnetic Resonance Imaging; D013154:Spleen / Q000201:enzymology
D015415:Biomarkers; D006596:Hexosaminidases; C086400:chitotriosidase; D005962:Glucosylceramidase; C090568:imiglucerase