title: Lentiviral vectors containing a retinal pigment epithelium specific promoter for leber congenital amaurosis gene therapy. Lentiviral gene therapy for LCA.
authors.affiliation: Oculogenetics Unit, Hôpital Ophtalmique Jules Gonin, Lausanne, Switzerland.
authors.forename: Alexis-Pierre
authors.initials: AP
authors.lastname: Bemelmans
authors.forename: Corinne
authors.initials: C
authors.lastname: Kostic
authors.forename: Dana
authors.initials: D
authors.lastname: Hornfeld
authors.forename: Muriel
authors.initials: M
authors.lastname: Jaquet
authors.forename: Sylvain V
authors.initials: SV
authors.lastname: Crippa
authors.forename: William W
authors.initials: WW
authors.lastname: Hauswirth
authors.forename: Janis
authors.initials: J
authors.lastname: Lem
authors.forename: Zhongyan
authors.initials: Z
authors.lastname: Wang
authors.forename: Daniel E
authors.initials: DE
authors.lastname: Schorderet
authors.forename: Francis L
authors.initials: FL
authors.lastname: Munier
authors.forename: Andreas
authors.initials: A
authors.lastname: Wenzel
authors.forename: Yvan
authors.initials: Y
authors.lastname: Arsenijevic
mesh_terms: D000818:Animals; D002352:Carrier Proteins / Q000235:genetics; D004596:Electroretinography / Q000379:methods; D005136:Eye Proteins / Q000235:genetics; D015316:Genetic Therapy / Q000379:methods*; D005822:Genetic Vectors; D049452:Green Fluorescent Proteins / Q000378:metabolism; D006801:Humans; D016086:Lentivirus / Q000235:genetics* / Q000378:metabolism; D051379:Mice; D018345:Mice, Knockout; D029242:Optic Atrophy, Hereditary, Leber / Q000235:genetics* / Q000628:therapy*; D010857:Pigment Epithelium of Eye / Q000378:metabolism*; D011401:Promoter Regions, Genetic; D012160:Retina / Q000378:metabolism; D019745:cis-trans-Isomerases; D000099178:Retinoid Isomerohydrolase
chemical_list: D002352:Carrier Proteins; D005136:Eye Proteins; D049452:Green Fluorescent Proteins; D019745:cis-trans-Isomerases; D000099178:Retinoid Isomerohydrolase