First treatment for Pompe disease.
D002675:Child, Preschool; D017277:Drug Approval; D004348:Drug Labeling; D006009:Glycogen Storage Disease Type II / Q000188:drug therapy*; D006801:Humans; D007223:Infant; D009965:Orphan Drug Production; D000520:alpha-Glucosidases / Q000009:adverse effects / Q000627:therapeutic use*
C509951:GAA protein, human; D000520:alpha-Glucosidases