Early marrow transplantation in a pre-symptomatic neonate with late infantile metachromatic leukodystrophy does not halt disease progression.
Bredius
R G M
RG
Laan
L A E M
LA
Lankester
A C
AC
Poorthuis
B J H M
BJ
van Tol
M J D
MJ
Egeler
R M
RM
Arts
W F M
WF
D016026:Bone Marrow Transplantation; D002675:Child, Preschool; D005260:Female; D006801:Humans; D007231:Infant, Newborn; D007966:Leukodystrophy, Metachromatic / Q000628:therapy*; D008297:Male; D012074:Remission Induction; D014184:Transplantation, Homologous