Hematopoietic cell therapy for metabolic disease.
Orchard
Paul J
PJ
Division of Hematology/Oncology and Blood and Marrow Transplantation, Department of Pediatrics, University of Minnesota, Minneapolis, MN 55455, USA. orcha001@umn.edu
Blazar
Bruce R
BR
Wagner
John
J
Charnas
Lawrence
L
Krivit
William
W
Tolar
Jakub
J
D000326:Adrenoleukodystrophy / Q000628:therapy; D018380:Hematopoietic Stem Cell Transplantation; D006801:Humans; D016464:Lysosomal Storage Diseases / Q000201:enzymology / Q000628:therapy*; D009083:Mucopolysaccharidoses / Q000628:therapy; D013106:Sphingolipidoses / Q000628:therapy; D016019:Survival Analysis