New LSD therapies unfolding.
NIH researchers report results of a qHTS hunt for new chemical chaperones for the treatment of Gaucher disease.
Kozarich
John W
JW
ActivX Biosciences, Incorporated, 11025 North Torrey Pines Road, La Jolla, CA 92037, USA. johnk@activx.com
D004353:Drug Evaluation, Preclinical / Q000379:methods; D005776:Gaucher Disease / Q000188:drug therapy*; D005962:Glucosylceramidase / Q000737:chemistry / Q000235:genetics; D006801:Humans; D009154:Mutation; D017510:Protein Folding
D005962:Glucosylceramidase