Progress and problems when considering gene therapy for GSD-II.
Kiang
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A
Department of Microbiology and Molecular Genetics, Michigan State University, East Lansing, MI 48824, USA.
Amalfitano
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A
D015316:Genetic Therapy / Q000639:trends*; D006009:Glycogen Storage Disease Type II / Q000201:enzymology / Q000235:genetics*; D006801:Humans; D011956:Receptors, Cell Surface / Q000235:genetics; D000520:alpha-Glucosidases / Q000235:genetics
D011956:Receptors, Cell Surface; C509951:GAA protein, human; D000520:alpha-Glucosidases