No justification for very high-dose enzyme therapy for patients with type III Gaucher disease.
Zimran
Ari
A
Elstein
Deborah
D
D002986:Clinical Trials as Topic; D004334:Drug Administration Schedule; D005776:Gaucher Disease / Q000188:drug therapy*; D005962:Glucosylceramidase / Q000627:therapeutic use*; D006801:Humans; D016896:Treatment Outcome
D005962:Glucosylceramidase