title: Gene therapy for mouse models of ADRP.
authors.affiliation: Department of Molecular Genetics and Microbiology, University of Florida College of Medicine, Gainesville 32610-0266, USA. mari653@mgm.ufl.edu
authors.forename: Marina S
authors.initials: MS
authors.lastname: Gorbatyuk
authors.forename: William W
authors.initials: WW
authors.lastname: Hauswirth
authors.forename: Alfred S
authors.initials: AS
authors.lastname: Lewin
mesh_terms: D000818:Animals; D002460:Cell Line; D004596:Electroretinography; D005799:Genes, Dominant; D015316:Genetic Therapy / Q000379:methods*; D006801:Humans; D007668:Kidney / Q000166:cytology; D008565:Membrane Proteins / Q000235:genetics*; D051379:Mice; D023421:Models, Animal; D000070780:Perilipin-2; D016337:RNA, Catalytic / Q000378:metabolism; D012333:RNA, Messenger / Q000378:metabolism; D034741:RNA, Small Interfering / Q000378:metabolism; D012174:Retinitis Pigmentosa / Q000209:etiology / Q000235:genetics*
chemical_list: D008565:Membrane Proteins; C000602982:PLIN2 protein, human; D000070780:Perilipin-2; C000602983:Plin2 protein, mouse; D016337:RNA, Catalytic; D012333:RNA, Messenger; D034741:RNA, Small Interfering