[Restoration of human dystrophin following transplantation of exon-skipping-engineered DMD patient stem cells into dystrophic mice].
Benchaouir
Rachid
R
Stem Cell Laboratory, Department of Neurological Sciences, Fondazione IRCCS Ospedale Maggiore Policlinico, Centro Dino Ferrari, University of Milan, via F. Sforza 35, Milan, Italy.
Meregalli
Mirella
M
Farini
Andrea
A
D'Antona
Giuseppe
G
Belicchi
Marzia
M
Goyenvalle
Aurélie
A
Battistelli
Maurizio
M
Bresolin
Nereo
N
Bottinelli
Roberto
R
Garcia
Luis
L
Torrente
Yvan
Y
D000818:Animals; D016189:Dystrophin / Q000235:genetics*; D005091:Exons; D005818:Genetic Engineering; D006801:Humans; D051379:Mice; D009137:Muscular Dystrophy, Animal / Q000235:genetics* / Q000628:therapy*; D020388:Muscular Dystrophy, Duchenne / Q000473:pathology*; D033581:Stem Cell Transplantation; D014183:Transplantation, Heterologous
D016189:Dystrophin