title: [Restoration of human dystrophin following transplantation of exon-skipping-engineered DMD patient stem cells into dystrophic mice].
authors.affiliation: Stem Cell Laboratory, Department of Neurological Sciences, Fondazione IRCCS Ospedale Maggiore Policlinico, Centro Dino Ferrari, University of Milan, via F. Sforza 35, Milan, Italy.
authors.forename: Rachid
authors.initials: R
authors.lastname: Benchaouir
authors.forename: Mirella
authors.initials: M
authors.lastname: Meregalli
authors.forename: Andrea
authors.initials: A
authors.lastname: Farini
authors.forename: Giuseppe
authors.initials: G
authors.lastname: D'Antona
authors.forename: Marzia
authors.initials: M
authors.lastname: Belicchi
authors.forename: Aurélie
authors.initials: A
authors.lastname: Goyenvalle
authors.forename: Maurizio
authors.initials: M
authors.lastname: Battistelli
authors.forename: Nereo
authors.initials: N
authors.lastname: Bresolin
authors.forename: Roberto
authors.initials: R
authors.lastname: Bottinelli
authors.forename: Luis
authors.initials: L
authors.lastname: Garcia
authors.forename: Yvan
authors.initials: Y
authors.lastname: Torrente
mesh_terms: D000818:Animals; D016189:Dystrophin / Q000235:genetics*; D005091:Exons; D005818:Genetic Engineering; D006801:Humans; D051379:Mice; D009137:Muscular Dystrophy, Animal / Q000235:genetics* / Q000628:therapy*; D020388:Muscular Dystrophy, Duchenne / Q000473:pathology*; D033581:Stem Cell Transplantation; D014183:Transplantation, Heterologous
chemical_list: D016189:Dystrophin