On the road to gene therapy for beta-thalassemia and sickle cell anemia.
Human globin gene therapy is a potential cure for sickle cell disease and beta-thalassemia (Cooley anemia). A clinical trial of this treatment is currently under way in Paris using lentiglobin vectors.
Bank
Arthur
A
Columbia University, New York, New York 10032, USA. ab13@columbia.edu
D000755:Anemia, Sickle Cell / Q000628:therapy*; D015316:Genetic Therapy / Q000379:methods*; D005822:Genetic Vectors; D005914:Globins / Q000235:genetics; D006801:Humans; D017086:beta-Thalassemia / Q000628:therapy*
D005914:Globins