title: Gene-targeted therapies for the central nervous system.
authors.affiliation: Neurosciences Department, University of California, San Diego, San Diego, California, USA. millert@neuro.wustl.edu
authors.forename: Timothy M
authors.initials: TM
authors.lastname: Miller
authors.forename: Richard A
authors.initials: RA
authors.lastname: Smith
authors.forename: Holly
authors.initials: H
authors.lastname: Kordasiewicz
authors.forename: Brian K
authors.initials: BK
authors.lastname: Kaspar
mesh_terms: D000818:Animals; D002493:Central Nervous System Diseases / Q000235:genetics / Q000628:therapy*; D004195:Disease Models, Animal; D005786:Gene Expression Regulation / Q000235:genetics; D018390:Gene Targeting / Q000379:methods*; D005822:Genetic Vectors / Q000235:genetics; D020271:Heredodegenerative Disorders, Nervous System / Q000235:genetics / Q000628:therapy*; D006801:Humans; D035683:MicroRNAs / Q000235:genetics; D016376:Oligonucleotides, Antisense / Q000235:genetics; D012333:RNA, Messenger / Q000235:genetics; D034741:RNA, Small Interfering / Q000235:genetics; D016896:Treatment Outcome
chemical_list: D035683:MicroRNAs; D016376:Oligonucleotides, Antisense; D012333:RNA, Messenger; D034741:RNA, Small Interfering