Lysosomal storage diseases: new challenges.
Scarpa
Maurizio
M
Department of Pediatrics, University of Padova, Padova, Italy. maurizio.scarpa@unipd.it
Eto
Yoshikatsu
Y
D000818:Animals; D004195:Disease Models, Animal; D015316:Genetic Therapy; D016464:Lysosomal Storage Diseases / Q000503:physiopathology / Q000628:therapy*