Clinical trials of orphan medicines.
Buckley
Brendan M
BM
European Centre for Clinical Trials in Rare Diseases, University College Cork, Cork, Ireland. b.buckley@ucc.ie
D002985:Clinical Protocols / Q000592:standards*; D002986:Clinical Trials as Topic / Q000379:methods* / Q000706:statistics & numerical data; D017277:Drug Approval; D006801:Humans; D009965:Orphan Drug Production; D035583:Rare Diseases / Q000145:classification / Q000188:drug therapy*; D018401:Sample Size