Gene therapy of inherited diseases.
Fischer
Alain
A
INSERM Unit 768, Paris, France. alain.fi scher@nck.ap-hop-paris.fr
Cavazzana-Calvo
Marina
M
D002986:Clinical Trials as Topic; D015316:Genetic Therapy / Q000379:methods* / Q000639:trends; D018380:Hematopoietic Stem Cell Transplantation / Q000379:methods* / Q000639:trends; D006801:Humans; D035583:Rare Diseases / Q000235:genetics* / Q000628:therapy