Why rare diseases are an important medical and social issue.
Schieppati
Arrigo
A
Clinical Research Centre for Rare Disease Aldo e Cele Daccò, Mario Negri Institute for Pharmacological Research, Bergamo, Italy. raredis@marionegri.it
Henter
Jan-Inge
JI
Daina
Erica
E
Aperia
Anita
A
D006801:Humans; D009965:Orphan Drug Production / Q000331:legislation & jurisprudence*; D015995:Prevalence; D011788:Quality of Life; D035583:Rare Diseases / Q000188:drug therapy / Q000453:epidemiology* / Q000235:genetics; D012941:Social Responsibility; D014481:United States