title: Patient page. Gene therapy and muscular dystrophies.
authors.forename: Steven
authors.initials: S
authors.lastname: Karceski
mesh_terms: D000818:Animals; D004195:Disease Models, Animal; D016189:Dystrophin / Q000096:biosynthesis / Q000172:deficiency / Q000235:genetics; D015316:Genetic Therapy / Q000379:methods / Q000639:trends*; D005822:Genetic Vectors / Q000235:genetics; D006801:Humans; D051379:Mice; D008967:Molecular Biology / Q000379:methods / Q000639:trends*; D009124:Muscle Proteins / Q000172:deficiency* / Q000235:genetics*; D009136:Muscular Dystrophies / Q000235:genetics* / Q000503:physiopathology / Q000628:therapy*; D049288:Muscular Dystrophies, Limb-Girdle / Q000235:genetics / Q000503:physiopathology / Q000628:therapy; D049031:Sarcoglycans / Q000172:deficiency / Q000235:genetics
chemical_list: D016189:Dystrophin; D009124:Muscle Proteins; D049031:Sarcoglycans