title: A "nema" of hope in the treatment of late-onset nemaline myopathy.
authors.forename: Marinos C
authors.initials: MC
authors.lastname: Dalakas
authors.forename: Stephen A
authors.initials: SA
authors.lastname: Smith
mesh_terms: D000328:Adult; D017668:Age of Onset; D002986:Clinical Trials as Topic; D006801:Humans; D008558:Melphalan / Q000627:therapeutic use; D019653:Myeloablative Agonists / Q000627:therapeutic use; D017696:Myopathies, Nemaline / Q000628:therapy*; D033581:Stem Cell Transplantation
chemical_list: D019653:Myeloablative Agonists; D008558:Melphalan