A "nema" of hope in the treatment of late-onset nemaline myopathy.
Dalakas
Marinos C
MC
Smith
Stephen A
SA
D000328:Adult; D017668:Age of Onset; D002986:Clinical Trials as Topic; D006801:Humans; D008558:Melphalan / Q000627:therapeutic use; D019653:Myeloablative Agonists / Q000627:therapeutic use; D017696:Myopathies, Nemaline / Q000628:therapy*; D033581:Stem Cell Transplantation
D019653:Myeloablative Agonists; D008558:Melphalan