Towards harmonisation of outcome measures for DMD and SMA within TREAT-NMD; report of three expert workshops: TREAT-NMD/ENMC workshop on outcome measures, 12th--13th May 2007, Naarden, The Netherlands; TREAT-NMD workshop on outcome measures in experimental trials for DMD, 30th June--1st July 2007, Naarden, The Netherlands; conjoint Institute of Myology TREAT-NMD meeting on physical activity monitoring in neuromuscular disorders, 11th July 2007, Paris, France.
Mercuri
E
E
Department of Paediatric Neurology, Catholic University, Rome, Italy. mercuri@rm.unicatt.it
Mayhew
A
A
Muntoni
F
F
Messina
S
S
Straub
V
V
Van Ommen
G J
GJ
Voit
T
T
Bertini
E
E
Bushby
K
K
D000818:Animals; D002986:Clinical Trials as Topic; D006801:Humans; D009048:Motor Skills / Q000502:physiology; D009134:Muscular Atrophy, Spinal / Q000503:physiopathology / Q000628:therapy*; D020388:Muscular Dystrophy, Duchenne / Q000503:physiopathology / Q000628:therapy*; D009468:Neuromuscular Diseases / Q000503:physiopathology / Q000628:therapy*; D017063:Outcome Assessment, Health Care