title: Towards harmonisation of outcome measures for DMD and SMA within TREAT-NMD; report of three expert workshops: TREAT-NMD/ENMC workshop on outcome measures, 12th--13th May 2007, Naarden, The Netherlands; TREAT-NMD workshop on outcome measures in experimental trials for DMD, 30th June--1st July 2007, Naarden, The Netherlands; conjoint Institute of Myology TREAT-NMD meeting on physical activity monitoring in neuromuscular disorders, 11th July 2007, Paris, France.
authors.affiliation: Department of Paediatric Neurology, Catholic University, Rome, Italy. mercuri@rm.unicatt.it
authors.forename: E
authors.initials: E
authors.lastname: Mercuri
authors.forename: A
authors.initials: A
authors.lastname: Mayhew
authors.forename: F
authors.initials: F
authors.lastname: Muntoni
authors.forename: S
authors.initials: S
authors.lastname: Messina
authors.forename: V
authors.initials: V
authors.lastname: Straub
authors.forename: G J
authors.initials: GJ
authors.lastname: Van Ommen
authors.forename: T
authors.initials: T
authors.lastname: Voit
authors.forename: E
authors.initials: E
authors.lastname: Bertini
authors.forename: K
authors.initials: K
authors.lastname: Bushby
mesh_terms: D000818:Animals; D002986:Clinical Trials as Topic; D006801:Humans; D009048:Motor Skills / Q000502:physiology; D009134:Muscular Atrophy, Spinal / Q000503:physiopathology / Q000628:therapy*; D020388:Muscular Dystrophy, Duchenne / Q000503:physiopathology / Q000628:therapy*; D009468:Neuromuscular Diseases / Q000503:physiopathology / Q000628:therapy*; D017063:Outcome Assessment, Health Care