title: New treatments for neuromuscular disease: optimism and obstacles.
authors.forename: Hanns
authors.initials: H
authors.lastname: Lochmüller
authors.forename: Robert C
authors.initials: RC
authors.lastname: Griggs
mesh_terms: D000818:Animals; D002986:Clinical Trials as Topic; D004195:Disease Models, Animal; D006801:Humans; D009468:Neuromuscular Diseases / Q000235:genetics / Q000473:pathology / Q000628:therapy*; D012107:Research Design