Age-related efficacy with an AAV vector in Fabry disease mice.
Koeberl
Dwight D
DD
Department of Pediatrics, Division of Medical Genetics, Duke University Medical Center, DUMC Box 103856, Durham, NC 27710, USA.
D000367:Age Factors; D000818:Animals; D000229:Dependovirus / Q000235:genetics* / Q000378:metabolism; D000795:Fabry Disease / Q000235:genetics* / Q000378:metabolism / Q000628:therapy*; D015316:Genetic Therapy; D005822:Genetic Vectors / Q000008:administration & dosage* / Q000378:metabolism; D006801:Humans; D051379:Mice