Dosing enzyme replacement therapy for Gaucher disease: older, but are we wiser?
Sidransky
Ellen
E
Medical Genetics Branch, National Human Genome Research Institute, National Institutes of Health, Bethesda, Maryland, USA. sidranse@mail.nih.gov
Pastores
Gregory M
GM
Mori
Motomi
M
D005776:Gaucher Disease / Q000188:drug therapy*; D005962:Glucosylceramidase / Q000627:therapeutic use; D006801:Humans; D016896:Treatment Outcome
D005962:Glucosylceramidase