title: Dosing enzyme replacement therapy for Gaucher disease: older, but are we wiser?
authors.affiliation: Medical Genetics Branch, National Human Genome Research Institute, National Institutes of Health, Bethesda, Maryland, USA. sidranse@mail.nih.gov
authors.forename: Ellen
authors.initials: E
authors.lastname: Sidransky
authors.forename: Gregory M
authors.initials: GM
authors.lastname: Pastores
authors.forename: Motomi
authors.initials: M
authors.lastname: Mori
mesh_terms: D005776:Gaucher Disease / Q000188:drug therapy*; D005962:Glucosylceramidase / Q000627:therapeutic use; D006801:Humans; D016896:Treatment Outcome
chemical_list: D005962:Glucosylceramidase