title: [Progress on lysosomal diseases yields hope for cure and improvement].
authors.affiliation: Sektionen för barnneurologi och habilitering, Barnens sjukhus, Karolinska Universitetssjukhuset Huddinge, Stockholm. gunilla.malm@karolinska.se
authors.forename: Gunilla
authors.initials: G
authors.lastname: Malm
authors.forename: Ulrika
authors.initials: U
authors.lastname: von Döbeln
authors.forename: Karin
authors.initials: K
authors.lastname: Naess
authors.forename: Olle
authors.initials: O
authors.lastname: Ringdén
mesh_terms: D002648:Child; D018450:Disease Progression; D042241:Early Diagnosis; D004789:Enzyme Activation / Q000187:drug effects; D006801:Humans; D016464:Lysosomal Storage Diseases / Q000145:classification / Q000175:diagnosis / Q000628:therapy; D011379:Prognosis; D033581:Stem Cell Transplantation