[Progress on lysosomal diseases yields hope for cure and improvement].
Malm
Gunilla
G
Sektionen för barnneurologi och habilitering, Barnens sjukhus, Karolinska Universitetssjukhuset Huddinge, Stockholm. gunilla.malm@karolinska.se
von Döbeln
Ulrika
U
Naess
Karin
K
Ringdén
Olle
O
D002648:Child; D018450:Disease Progression; D042241:Early Diagnosis; D004789:Enzyme Activation / Q000187:drug effects; D006801:Humans; D016464:Lysosomal Storage Diseases / Q000145:classification / Q000175:diagnosis / Q000628:therapy; D011379:Prognosis; D033581:Stem Cell Transplantation