Gene therapy in large animal models of human genetic diseases. Introduction.
Wolfe
John H
JH
WF Goodman Center for Comparative Medical Genetics at the University of Pennsylvania School of Veterinary Medicine and Stokes Investigator at the Children's Hospital of Philadelphia, PA 19104, USA. jhwolfe@vet.upenn.edu
D000818:Animals; D004195:Disease Models, Animal; D018014:Gene Transfer Techniques; D030342:Genetic Diseases, Inborn / Q000235:genetics* / Q000628:therapy*; D015316:Genetic Therapy / Q000379:methods*