Exon skipping, a therapy for Duchenne muscular dystrophy. Interview by Guenter Scheuerbrandt.
Gerard
G
Platenburg
D002986:Clinical Trials as Topic; D015195:Drug Design; D005091:Exons; D015316:Genetic Therapy / Q000379:methods; D006801:Humans; D020388:Muscular Dystrophy, Duchenne / Q000188:drug therapy* / Q000235:genetics*; D009154:Mutation; D016376:Oligonucleotides, Antisense / Q000235:genetics / Q000494:pharmacology* / Q000627:therapeutic use*
D016376:Oligonucleotides, Antisense