PTC124 for cystic fibrosis.
Goodier
John L
JL
Mayer
Jens
J
D018389:Codon, Nonsense / Q000187:drug effects*; D018388:Codon, Terminator / Q000187:drug effects*; D003550:Cystic Fibrosis / Q000188:drug therapy* / Q000235:genetics; D015316:Genetic Therapy / Q000009:adverse effects; D006801:Humans; D010069:Oxadiazoles / Q000009:adverse effects / Q000494:pharmacology*; D018626:Retroelements / Q000187:drug effects*
D018389:Codon, Nonsense; D018388:Codon, Terminator; D010069:Oxadiazoles; D018626:Retroelements; C515878:ataluren