Musings on genome medicine: gene therapy.
Though the field has moved with glacial speed, gene therapies have been carried out successfully in patients with bone marrow disorders including immune deficiencies. The field may be poised to move forward more rapidly, but many barriers have yet to be surmounted.
Nathan
David G
DG
Dana-Farber Cancer Institute, Binney Street, Boston, MA 02115, USA,. david_nathan@dfci.harvard.edu.
Orkin
Stuart H
SH