Outcome measures in Duchenne muscular dystrophy: are we ready for the new therapeutic era?
Merkies
Ingemar S J
IS
Department of Neurology, University Hospital Maastricht, P.O. Box 5800, Maastricht, The Netherlands. stapscot@fhcrc.org
Faber
Catharina G
CG
D006801:Humans; D020388:Muscular Dystrophy, Duchenne / Q000175:diagnosis* / Q000628:therapy*; D012720:Severity of Illness Index; D016896:Treatment Outcome