Gene therapy for hemophilia A. Friend or foe?
Lippi
Giuseppe
G
Section of Clinical Chemistry, Department of Biomedical and Morphological Sciences, University of Verona, Verona, Italy. ulippi@tin.it
Franchini
Massimo
M
Saenko
Evgueni L
EL
D000818:Animals; D004251:DNA Transposable Elements; D004195:Disease Models, Animal; D004285:Dogs; D005169:Factor VIII / Q000235:genetics / Q000276:immunology / Q000627:therapeutic use*; D005544:Forecasting; D015316:Genetic Therapy / Q000009:adverse effects; D005822:Genetic Vectors / Q000627:therapeutic use / Q000633:toxicity; D006467:Hemophilia A / Q000235:genetics / Q000628:therapy*; D006801:Humans; D008251:Macaca; D008297:Male; D051379:Mice; D016688:Mice, Inbred NOD; D008815:Mice, Inbred Strains; D018345:Mice, Knockout; D016513:Mice, SCID; D015202:Protein Engineering; D011993:Recombinant Fusion Proteins / Q000235:genetics / Q000627:therapeutic use; D012190:Retroviridae / Q000235:genetics / Q000502:physiology; D013045:Species Specificity
D004251:DNA Transposable Elements; D011993:Recombinant Fusion Proteins; C078147:F8 protein, human; D005169:Factor VIII