title: My child has Leber congenital amaurosis: why is he/she not eligible for gene therapy trials?
authors.forename: Elise
authors.initials: E
authors.lastname: Héon
mesh_terms: D002352:Carrier Proteins / Q000235:genetics; D002648:Child; D002675:Child, Preschool; D002986:Clinical Trials as Topic; D005136:Eye Proteins / Q000235:genetics; D005260:Female; D015316:Genetic Therapy; D006801:Humans; D057130:Leber Congenital Amaurosis / Q000175:diagnosis / Q000235:genetics / Q000628:therapy*; D008297:Male; D018579:Patient Selection; D019745:cis-trans-Isomerases; D000099178:Retinoid Isomerohydrolase
chemical_list: D002352:Carrier Proteins; D005136:Eye Proteins; D019745:cis-trans-Isomerases; D000099178:Retinoid Isomerohydrolase