title: Medicine. A comeback for gene therapy.
authors.affiliation: San Raffaele Telethon Institute for Gene Therapy, Vita Salute San Raffaele University, Via Olgettina, 58, 20132 Milano, 20132 Italy. naldini.luigi@hsr.it
authors.forename: Luigi
authors.initials: L
authors.lastname: Naldini
mesh_terms: D000074063:ATP Binding Cassette Transporter, Subfamily D, Member 1; D018528:ATP-Binding Cassette Transporters / Q000235:genetics*; D000326:Adrenoleukodystrophy / Q000235:genetics / Q000628:therapy*; D002648:Child; D018450:Disease Progression; D015870:Gene Expression; D015316:Genetic Therapy; D005822:Genetic Vectors; D015497:HIV-1 / Q000235:genetics* / Q000502:physiology; D006410:Hematopoiesis; D018380:Hematopoietic Stem Cell Transplantation; D006412:Hematopoietic Stem Cells / Q000502:physiology* / Q000821:virology; D006801:Humans; D008297:Male; D014161:Transduction, Genetic; D014182:Transplantation, Autologous; D016662:Virus Integration
chemical_list: C115572:ABCD1 protein, human; D000074063:ATP Binding Cassette Transporter, Subfamily D, Member 1; D018528:ATP-Binding Cassette Transporters