Gene therapy. Beta-thalassemia treatment succeeds, with a caveat.
Kaiser
Jocelyn
J
D049109:Cell Proliferation; D002986:Clinical Trials as Topic; D015316:Genetic Therapy; D005822:Genetic Vectors; D025743:HMGA2 Protein / Q000235:genetics; D006454:Hemoglobins / Q000032:analysis; D006801:Humans; D008297:Male; D014481:United States; D055815:Young Adult; D055544:beta-Globins / Q000096:biosynthesis / Q000235:genetics*; D017086:beta-Thalassemia / Q000235:genetics / Q000628:therapy*
D025743:HMGA2 Protein; D006454:Hemoglobins; D055544:beta-Globins