title: Novel therapies and future perspectives.
authors.affiliation: Department of Pediatrics, University of Padova, Padova, Italy. maurizio.scarpa@unipd.it
authors.forename: M
authors.initials: M
authors.lastname: Scarpa
authors.forename: A
authors.initials: A
authors.lastname: Frustaci
mesh_terms: D056947:Enzyme Replacement Therapy / Q000379:methods*; D015316:Genetic Therapy / Q000379:methods; D006801:Humans; D016464:Lysosomal Storage Diseases / Q000628:therapy*; D018832:Molecular Chaperones / Q000627:therapeutic use
chemical_list: D018832:Molecular Chaperones