Novel therapies and future perspectives.
Scarpa
M
M
Department of Pediatrics, University of Padova, Padova, Italy. maurizio.scarpa@unipd.it
Frustaci
A
A
D056947:Enzyme Replacement Therapy / Q000379:methods*; D015316:Genetic Therapy / Q000379:methods; D006801:Humans; D016464:Lysosomal Storage Diseases / Q000628:therapy*; D018832:Molecular Chaperones / Q000627:therapeutic use
D018832:Molecular Chaperones