[Update on RNA splicing repair: applications to beta thalassemia and other perspectives].
Dominique
D
Labie
Jean-Claude
JC
Kaplan
D000818:Animals; D005091:Exons / Q000235:genetics; D015316:Genetic Therapy / Q000379:methods*; D005822:Genetic Vectors / Q000009:adverse effects / Q000627:therapeutic use; D006801:Humans; D016086:Lentivirus / Q000235:genetics; D051379:Mice; D008822:Mice, Transgenic; D009136:Muscular Dystrophies / Q000235:genetics / Q000628:therapy; D016376:Oligonucleotides, Antisense / Q000235:genetics / Q000494:pharmacology / Q000627:therapeutic use*; D022821:RNA Splice Sites / Q000235:genetics*; D012326:RNA Splicing / Q000187:drug effects* / Q000235:genetics; D055542:alpha-Globins / Q000037:antagonists & inhibitors / Q000235:genetics; D017086:beta-Thalassemia / Q000235:genetics / Q000628:therapy*
D016376:Oligonucleotides, Antisense; D022821:RNA Splice Sites; D055542:alpha-Globins