title: Rare opportunities appear on the horizon to treat rare diseases.
authors.forename: Christian
authors.initials: C
authors.lastname: Torres
mesh_terms: D004345:Drug Industry; D006801:Humans; D009965:Orphan Drug Production / Q000331:legislation & jurisprudence*; D035583:Rare Diseases / Q000188:drug therapy*; D014481:United States; D014486:United States Food and Drug Administration