title: Genetic therapy for spinal muscular atrophy.
authors.forename: Alex
authors.initials: A
authors.lastname: MacKenzie
mesh_terms: D000818:Animals; D002648:Child; D015316:Genetic Therapy / Q000379:methods*; D006801:Humans; D007223:Infant; D051379:Mice; D008822:Mice, Transgenic; D009046:Motor Neurons / Q000473:pathology; D009134:Muscular Atrophy, Spinal / Q000235:genetics / Q000473:pathology / Q000628:therapy*; D055533:Survival of Motor Neuron 1 Protein / Q000235:genetics; D055540:Survival of Motor Neuron 2 Protein / Q000235:genetics
chemical_list: D055533:Survival of Motor Neuron 1 Protein; D055540:Survival of Motor Neuron 2 Protein