title: [Benefits of early enzyme replacement therapy in two children with type 1 Gaucher disease].
authors.affiliation: Service de Pédiatrie, Hématologie-Oncologie, Pôle Enfants, Hôpital des Enfants, 330 avenue de Grande Bretagne, TSA 70034, 31059 Toulouse cedex 9, France. robert.a@chu-toulouse.fr
authors.forename: Alain
authors.initials: A
authors.lastname: Robert
mesh_terms: D000293:Adolescent; D000367:Age Factors; D056947:Enzyme Replacement Therapy; D005260:Female; D005776:Gaucher Disease / Q000188:drug therapy*; D006801:Humans; D008297:Male
vernacular_title: Bénéfice du traitement enzymatique substitutif précoce chez deux enfants atteints de maladie de Gaucher de type 1.