Spinal muscular atrophy disease: a literature review for therapeutic strategies.
Stavarachi
M
M
Human Genetics and Molecular Diagnosis Department, Institute of Genetics, 1-3 Portocalelor Street, District 6, postal code 060101, Bucharest, Romania. monica.stavarachi@gmail.com
Apostol
P
P
Toma
M
M
Cimponeriu
D
D
Gavrila
L
L
D045930:Anabolic Agents / Q000627:therapeutic use; D005091:Exons; D015316:Genetic Therapy; D006801:Humans; D009134:Muscular Atrophy, Spinal / Q000235:genetics / Q000628:therapy*; D018696:Neuroprotective Agents / Q000627:therapeutic use; D011401:Promoter Regions, Genetic; D033581:Stem Cell Transplantation; D055540:Survival of Motor Neuron 2 Protein / Q000235:genetics
D045930:Anabolic Agents; D018696:Neuroprotective Agents; C526477:SMN2 protein, human; D055540:Survival of Motor Neuron 2 Protein