Phase 1/2 and extension study of velaglucerase alfa replacement therapy in adults with type 1 Gaucher disease: 48-month experience.
Zimran
Ari
A
Gaucher Clinic, Shaare Zedek Medical Center, Jerusalem, Israel.
Altarescu
Gheona
G
Philips
Mici
M
Attias
Drorit
D
Jmoudiak
Marina
M
Deeb
Maher
M
Wang
Nan
N
Bhirangi
Kiran
K
Cohn
Gabriel M
GM
Elstein
Deborah
D
D000328:Adult; D000368:Aged; D056947:Enzyme Replacement Therapy; D005260:Female; D005776:Gaucher Disease / Q000188:drug therapy* / Q000473:pathology; D005962:Glucosylceramidase / Q000009:adverse effects / Q000627:therapeutic use*; D006801:Humans; D008297:Male; D008875:Middle Aged; D009929:Organ Size / Q000187:drug effects; D013154:Spleen / Q000473:pathology; D013997:Time Factors
D005962:Glucosylceramidase