The development of antisense oligonucleotide therapies for Duchenne muscular dystrophy: report on a TREAT-NMD workshop hosted by the European Medicines Agency (EMA), on September 25th 2009.
Muntoni
F
F
The Dubowitz Neuromuscular Centre, University College London, Institute of Child Health, 30 Guildford Street, London WC1N1EH, UK. f.muntoni@ich.ucl.ac.uk