Peripheral transvenular delivery of adeno-associated viral vectors to skeletal muscle as a novel therapy for hemophilia B.
Arruda
Valder R
VR
University of Pennsylvania School of Medicine, Philadelphia, PA, USA.
Stedman
Hansell H
HH
Haurigot
Virginia
V
Buchlis
George
G
Baila
Stefano
S
Favaro
Patricia
P
Chen
Yifeng
Y
Franck
Helen G
HG
Zhou
Shangzhen
S
Wright
J Fraser
JF
Couto
Linda B
LB
Jiang
Haiyan
H
Pierce
Glenn F
GF
Bellinger
Dwight A
DA
Mingozzi
Federico
F
Nichols
Timothy C
TC
High
Katherine A
KA