Innovative vector design: cross-packaged, self-complementary and now trans-splicing AAV vectors.
Byrne
Barry J
BJ
University of Florida, Powell Gene Therapy Center, Gainesville, FL 32610, USA. bbyrne@ufl.edu
D000229:Dependovirus / Q000235:genetics*; D015316:Genetic Therapy / Q000379:methods*; D005822:Genetic Vectors / Q000235:genetics*; D006801:Humans; D009468:Neuromuscular Diseases / Q000628:therapy*; D020040:Trans-Splicing / Q000235:genetics; D019076:Transgenes / Q000235:genetics*