Prognostic factors for late-onset Pompe disease with enzyme replacement therapy: The two sides of low BMI.
Ravaglia
Sabrina
S
Carlucci
Annalisa
A
Danesino
Cesare
C
D000328:Adult; D017668:Age of Onset; D015992:Body Mass Index; D056947:Enzyme Replacement Therapy; D006009:Glycogen Storage Disease Type II / Q000175:diagnosis* / Q000188:drug therapy / Q000453:epidemiology* / Q000503:physiopathology; D006801:Humans; D011379:Prognosis; D000520:alpha-Glucosidases / Q000627:therapeutic use
D000520:alpha-Glucosidases