title: An open-label Phase I/II clinical trial of pyrimethamine for the treatment of patients affected with chronic GM2 gangliosidosis (Tay-Sachs or Sandhoff variants).
authors.affiliation: Research Institute, Hospital for Sick Children, Toronto, Ontario, Canada. jtrc@sickkids.ca
authors.forename: Joe T R
authors.initials: JT
authors.lastname: Clarke
authors.forename: Don J
authors.initials: DJ
authors.lastname: Mahuran
authors.forename: Swati
authors.initials: S
authors.lastname: Sathe
authors.forename: Edwin H
authors.initials: EH
authors.lastname: Kolodny
authors.forename: Brigitte A
authors.initials: BA
authors.lastname: Rigat
authors.forename: Julian A
authors.initials: JA
authors.lastname: Raiman
authors.forename: Michael B
authors.initials: MB
authors.lastname: Tropak