Pharmacological small molecules for the treatment of lysosomal storage disorders.
Smid
B E
BE
Academical Medical Center, Internal Medicine/Department of Endocrinology and Metabolism, Meibergdreef 9, Amsterdam, Netherlands.
Aerts
J M F G
JM
Boot
R G
RG
Linthorst
G E
GE
Hollak
C E M
CE