title: Targeting the basic defect in cystic fibrosis.
authors.forename: Michael J
authors.initials: MJ
authors.lastname: Welsh
mesh_terms: D000627:Aminophenols / Q000627:therapeutic use*; D003550:Cystic Fibrosis / Q000188:drug therapy* / Q000235:genetics; D019005:Cystic Fibrosis Transmembrane Conductance Regulator / Q000235:genetics*; D006801:Humans; D007231:Infant, Newborn; D009154:Mutation; D015997:Neonatal Screening; D015363:Quinolones / Q000627:therapeutic use*
chemical_list: D000627:Aminophenols; C505032:CFTR protein, human; D015363:Quinolones; D019005:Cystic Fibrosis Transmembrane Conductance Regulator; C545203:ivacaftor