Autoimmunity, recessive diseases, and gene replacement therapy.
Department of Pathology and Laboratory Medicine, University of Pennsylvania, Philadelphia, Pennsylvania 19104, USA. wilsonjm@mail.med.upenn.edu
James M
JM
Wilson
D015551:Autoimmunity; D005808:Genes, Recessive / Q000235:genetics; D030342:Genetic Diseases, Inborn / Q000628:therapy*; D015316:Genetic Therapy; D006801:Humans