title: Early access experience with VPRIV(®): recommendations for 'core data' collection.
authors.forename: Derralynn A
authors.initials: DA
authors.lastname: Hughes
authors.forename: Moeen
authors.initials: M
authors.lastname: Al-Sayed
authors.forename: Nadia
authors.initials: N
authors.lastname: Belmatoug
authors.forename: Olaf
authors.initials: O
authors.lastname: Bodamer
authors.forename: Tobias
authors.initials: T
authors.lastname: Böttcher
authors.forename: Maria
authors.initials: M
authors.lastname: Cappellini
authors.forename: Ian J
authors.initials: IJ
authors.lastname: Cohen
authors.forename: Terence
authors.initials: T
authors.lastname: Eagleton
authors.forename: Deborah
authors.initials: D
authors.lastname: Elstein
authors.forename: Pilar
authors.initials: P
authors.lastname: Giraldo
authors.forename: Simon
authors.initials: S
authors.lastname: Jones
authors.forename: Chaim
authors.initials: C
authors.lastname: Kaplinsky
authors.forename: Allan
authors.initials: A
authors.lastname: Lund
authors.forename: Maciej
authors.initials: M
authors.lastname: Machaczka
authors.forename: Eugen
authors.initials: E
authors.lastname: Mengel
authors.forename: Gregory M
authors.initials: GM
authors.lastname: Pastores
authors.forename: Hanna
authors.initials: H
authors.lastname: Rosenbaum
authors.forename: Malvin
authors.initials: M
authors.lastname: Sjo
authors.forename: Nikolaus
authors.initials: N
authors.lastname: Tiling
authors.forename: Panagiotis
authors.initials: P
authors.lastname: Tsaftaridis
authors.forename: Ari
authors.initials: A
authors.lastname: Zimran
authors.forename: Neal
authors.initials: N
authors.lastname: Weinreb
mesh_terms: D002460:Cell Line; D003625:Data Collection / Q000592:standards; D056947:Enzyme Replacement Therapy / Q000941:ethics / Q000379:methods*; D005776:Gaucher Disease / Q000188:drug therapy* / Q000473:pathology; D005962:Glucosylceramidase / Q000008:administration & dosage / Q000096:biosynthesis / Q000627:therapeutic use*; D006801:Humans; D017410:Practice Guidelines as Topic / Q000592:standards; D011994:Recombinant Proteins / Q000008:administration & dosage / Q000096:biosynthesis / Q000627:therapeutic use*
chemical_list: D011994:Recombinant Proteins; D005962:Glucosylceramidase; C550184:Velaglucerase alfa, human