title: Trans-splicing, more than meets the eye: multifaceted therapeutics for spinal muscular atrophy.
authors.affiliation: Department of Molecular and Cellular Biochemistry, College of Medicine, Ohio State University , Columbus, OH 43210, USA. butchbach.1@osu.edu
authors.forename: Matthew E R
authors.initials: ME
authors.lastname: Butchbach
mesh_terms: D000818:Animals; D015870:Gene Expression; D015316:Genetic Therapy; D006801:Humans; D007334:Insulin-Like Growth Factor I / Q000378:metabolism; D051379:Mice; D008822:Mice, Transgenic; D009134:Muscular Atrophy, Spinal / Q000235:genetics* / Q000628:therapy*; D055533:Survival of Motor Neuron 1 Protein / Q000235:genetics; D055540:Survival of Motor Neuron 2 Protein / Q000235:genetics; D020040:Trans-Splicing
chemical_list: C526471:SMN1 protein, human; C526477:SMN2 protein, human; D055533:Survival of Motor Neuron 1 Protein; D055540:Survival of Motor Neuron 2 Protein; D007334:Insulin-Like Growth Factor I