title: Gene therapy finds its niche.
abstract: Gene therapy is finally poised to make a contribution to the treatment of debilitating, highly penetrant genetic diseases that have proved intractable to other regimens.
authors.forename: Cormac
authors.initials: C
authors.lastname: Sheridan
mesh_terms: D000328:Adult; D002648:Child; D002986:Clinical Trials as Topic; D015316:Genetic Therapy; D005822:Genetic Vectors; D006801:Humans