title: AAV6-mediated gene silencing fALS short.
authors.affiliation: Department of Neuroscience, McKnight Brain Institute, University of Florida College of Medicine, Gainesville, FL, USA. rmandel@mbi.ufl.edu
authors.forename: Ronald J
authors.initials: RJ
authors.lastname: Mandel
authors.forename: Pedro R
authors.initials: PR
authors.lastname: Lowenstein
authors.forename: Barry J
authors.initials: BJ
authors.lastname: Byrne
mesh_terms: D000690:Amyotrophic Lateral Sclerosis / Q000628:therapy; D000818:Animals; D000229:Dependovirus / Q000235:genetics*; D004195:Disease Models, Animal; D015316:Genetic Therapy / Q000379:methods; D005822:Genetic Vectors / Q000235:genetics*; D006801:Humans; D007273:Injections, Intramuscular; D051379:Mice; D008822:Mice, Transgenic; D009046:Motor Neurons / Q000378:metabolism; D034622:RNA Interference / Q000502:physiology; D034741:RNA, Small Interfering / Q000235:genetics / Q000502:physiology; D013482:Superoxide Dismutase / Q000235:genetics*; D000072105:Superoxide Dismutase-1
chemical_list: D034741:RNA, Small Interfering; C000606290:SOD1 protein, human; C000606291:Sod1 protein, mouse; D013482:Superoxide Dismutase; D000072105:Superoxide Dismutase-1